Rivals
PROJECT TITLE RIVALS study – evaluation of the efficacy of ofatumumab treatment in patients with refractory idiopathic inflammatory myopathies compared to subcutaneous immunoglobulins.
ViRap
Project title: Randomized, placebo-controlled, double-blind and double-dummy clinical trial comparing the safety, tolerability, and efficacy of vigabatrin and rapamycin in a preventive treatment of infants with Tuberous Sclerosis Complex (ViRap).
RaRE-TS
Project title: Multicenter, randomized, double-blind, placebocontrolledstudy to assess the efficacy and safety of Rapamycin in drug Resistant Epilepsy associated with TSC (RaRE-TS).
RemiRit
Project title: RemiRit – Personalized immunosuppressive therapy with rituximab in the treatment of ANCA associated vasculitis – a randomized, multicenter clinical trial.
Forma
Project title: FORMA – a multicentre randomized-controlled trial to evaluate the efficacy and safety of ketoanalogues of essential amino acids in prophylaxis of protein-energy wasting in nephrotic syndrome.
SHIELD-Fabry
Low-dose corticosteroids adjacent to enzyme replacement therapy or chaperon therapy in patients with cardiac manifestation of Fabry disease – prospective randomized controlled trial with cross-over (SHIELD-Fabry)