UMED as the Consortium Leader
Project name: SHIELD-Fabry
Project title: Low-dose corticosteroids adjacent to enzyme replacement therapy or chaperon therapy in patients with cardiac manifestation of Fabry disease - prospective randomized controlled trial with cross-over (SHIELD-Fabry)
Project name: PICOLO-FH trial
Project title: ComParison of InClisiran Or aLirOcumab to standard therapy in pediatric Familial Hypercholesterolemia – the head-to-head PICOLO-FH clinical trial
Project name: BOOSTER trial
Project title: B cell depletion therapy to improve outcomes of steroid-sensitive nephrotic syndrome in adults – the BOOSTER trial
What the study is about: idiopathic steroid-sensitive nephrotic syndrome (SSNS)
Project name: COMBO-UC trial
Project title: Comparison of ustekinumab, infliximab and COMBinatiOn therapy in moderately-to-severely active Ulcerative Colitis – the head to head COMBO-UC trial
What the study is about: Ulcerative colitis
Project name: LAMAinDiab
Project title: LAMAinDiab – lisdexamphetamine vs metylphenidate for pediatric patients with attention-deficit hyperactivity disorder and type 1 diabetes – randomized cross-over clinical trial
What the study is about: ADHD, type 1 diabetes
Project name: STEADY
Project title: Prospective, randomized, open-label Phase III clinical trial with blinded endpoint assessing the efficacy and safety of ciclosporin and methotrexate in children and adolescents with moderate to severe atopic dermatitis.
What the study is about: Atopic dermatitis (AD)
Project name: Alzheimer
Project title: Randomized, double-blind, placebo-controlled trial evaluating efficacy and safety of dimethyl fumarate in brain atrophy reduction, synaptic functional connectivity, cognitive functions, quality of life, and activity of daily living improvement among patients with mild cognitive impairment and dementia due to Alzheimer’s disease.
What the study is about: Alzheimer
Project name: MAGIC-AML
Project title: MAGIC-AML - Multiarm, Multicenter, RAndomized, Molecularly-GuIded Controlled Trial of Personalized Treatment Strategy - of Acute Myeloid Leukemia
What the study is about: AML, acute myeloid leukemia (AML)
Project name: cALL-POL
Project title: Childhood ALL in Poland (cALL-POL) project: a national harmonization of diagnostics and treatment of acute lymphoblastic leukemia in children
What the study is about: acute lymphoblastic leukemia (ALL)