UMED as a Consortium member/ Partner
Project name: TreatWolfram
Project title: An international, randomized, double-blinded, pivotal clinical trial with the aim to evaluate the efficacy and safety of sodium valproate in children and adults with Wolfram syndrome.
What the study is about: Wolfram syndrome
Project name: Interfant-21
Project title: International collaborative treatment protocol for infants under one year with KMT2A-rearranged acute lymphoblastic leukemia or mixed phenotype acute leukemia.
What the study is about: KMT2A-rearranged acute lymphoblastic leukemia or mixed phenotype acute leukemia in infants
Project name: EMPATHY
Project title: EMpagliflozin and daPAgliflozin in patients hospiTalized for acute decompensated Heart failure (EMPATHY trial)
What the study is about: acute heart failure (AHF)
Project name: Protect ICD
Project title: Programmed Ventricular Stimulation to Risk Stratify for Early Cardioverter-Defibrillator (ICD) Implantation to Prevent Tachyarrhythmias Following Acute Myocardial Infarction.
What the study is about: poor heart function after myocardial infarction (MI)
Project name: Forma
Project title: FORMA – a multicentre randomized-controlled trial to evaluate the efficacy and safety of ketoanalogues of essential amino acids in prophylaxis of protein-energy wasting in nephrotic syndrome.
What the study is about: eating disorders, nephrotic syndrome (NS)
Project name: RemiRit
Project title: RemiRit - Personalized immunosuppressive therapy with rituximab in the treatment of ANCA associated vasculitis - a randomized, multicenter clinical trial.
What the study is about: systemic vasculitis with the presence of ANCA antibodies
Project name: RaRE-TS
Project title: Multicenter, randomized, double-blind, placebocontrolledstudy to assess the efficacy and safety of Rapamycin in drug Resistant Epilepsy associated with TSC (RaRE-TS).
What the study is about: epilepsy, tuberous sclerosis
Project name: RATIONAL
Project title: A phase II efficacy and safety study of cell-free circulating tumor DNA-guided commencement of second-line treatment in patients with DLBCL/HGBCL relapse.
What the study is about: DLBCL / HGBCL lymphoma
Project name: Car-NET
Project title: Polish Chimeric Antigen Receptor T-cell Network
Project name: ViRap
Project title: Randomized, placebo-controlled, double-blind and double-dummy clinical trial comparing the safety, tolerability, and efficacy of vigabatrin and rapamycin in a preventive treatment of infants with Tuberous Sclerosis Complex (ViRap).
What the study is about: epilepsy, mental retardation, autism, tuberous sclerosis
Project name: LEIA-HF
Project title: LEIA-HF: Levosimendan In Ambulatory Heart Failure Patients
What the study is about: ciężka niewydolność serca (NS)